Thrombotic thrombocytopenic purpura

Synonyms: Moschcowitz disease | TTP

An aggressive and life-threatening form of thrombotic microangiopathy (TMA) characterized by profound peripheral thrombocytopenia microangiopathic hemolytic anemia (MAHA) and organ failure of variable severity and is comprised of a congenital (cTTP) and acquired immune-mediated (iTTP) form.

Data from Orphanet are used to provide information on a disease's name, synonym(s), and overview. Reference: Access aggregated data from Orphanet at Orphadata. Orphadata: Free access data from Orphanet. © INSERM 1999. Available on http://www.orphadata.org. Data version April 2026

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Thrombotic thrombocytopenic purpura

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Clinical Trials

Newly diagnosed with
Thrombotic thrombocytopenic purpura?